Pitt–Hopkins syndrome (PTHS)– a case report from Pakistan

Authors

  • Asghar Nasir Department of Pathology and Laboratory Medicine, Aga Khan University, Karachi, Pakistan
  • Bushra Afroze Department of Paediatrics and Child Health, Aga Khan University, Karachi, Pakistan
  • Saad Ilyas 4th Year MBBS Student, Aga Khan University, Karachi, Pakistan
  • Zeeshan Ansar Department of Pathology and Laboratory Medicine, Aga Khan University, Karachi, Pakistan
  • Zahra Hasan Department of Pathology and Laboratory Medicine, Aga Khan University, Karachi, Pakistan

DOI:

https://doi.org/10.47391/JPMA.30215

Keywords:

Pitt–Hopkins syndrome, TCF4 gene, Chromosomal Microarray Analysis, Pakistan case report

Abstract

Pitt–Hopkins syndrome (PTHS) is a rare genetic neurodevelopment disorder where affected individuals exhibit symptoms such as severe developmental delays and intellectual disability. To the best of our knowledge, this report presents the first known case from Pakistan where Chromosomal Microarray Analysis (CMA) was employed to diagnose PTHS. The CMA revealed a deletion in the Transcription Factor 4 (TCF4) gene, confirming the diagnosis. This case underscores the clinical features, diagnostic process, and the significance of CMA in diagnosing rare genetic disorders such as PTHS, particularly in resource-limited settings.

Keywords: Pitt–Hopkins syndrome, TCF4 gene, Chromosomal Microarray Analysis, Pakistan case report.

Published

2026-06-25

How to Cite

Nasir, A., Afroze, B., Ilyas, S., Ansar, Z., & Hasan, Z. (2026). Pitt–Hopkins syndrome (PTHS)– a case report from Pakistan. Journal of the Pakistan Medical Association, 76(07), 1163–1165. https://doi.org/10.47391/JPMA.30215

Issue

Section

CASE REPORT